How PMS began: the first 22q13 deletion case
Dr. Katy Phelan takes us back to the earliest days of identifying 22q13 deletions — and how discovery turned into collaboration, then community. Subscribe for monthly episodes. @GENErationHope_1 #22q13 #SHANK3 #Genetics #RareDisease #GEN...
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Gene Therapy Weekly: CRISPR's Biggest Trial Result Yet | GENEration Hope
Update for the week of April 27, 2026 A CRISPR-based treatment just delivered pivotal Phase 3 results for a rare and debilitating disease — and for rare disease families, this is a milestone worth understanding. This week, Ron breaks dow...
“If We Solve This… I’ll Be the Happiest Person” | Guoping Feng
Dr. Feng talks about the reality families live with — and what it would mean if we could truly treat severe neurodevelopmental disorders. Full interview on GENEration Hope.
“It’s Technical — We Can Solve It” | Why He’s Optimistic
Dr. Feng explains why many monogenic neurodevelopmental disorders feel solvable now — if we put enough people and resources behind them. Full interview on GENEration Hope.